Agenda
At the request of the DMD nominators, there will not be a vote for inclusion of Duchenne Muscular Dystrophy to the RUSP during the May meeting. Instead, the Committee will decide during the Thursday DMD agenda time what action to take, such as a vote to postpone a RUSP recommendation to a future meeting.
The meeting is currently scheduled to run Thursday, May 9, 2024, from 10:00 AM to 5:00 PM Eastern Time (ET) and Friday, May 10, 2024, from 10:00 AM to 3:00 PM (ET). A final agenda will be posted no later than 48 hours before the meeting.
Thursday, May 9, 2024 from 10:00 AM – 3:45 PM
(All times shown are in Eastern Time)
TIME | TOPIC |
10:00 AM – 10:15 AM |
|
10:15 AM – 11:00 AM | Public Comments |
11:00 AM – 11:10 AM | Break |
11:10 AM – 11:30 AM | Regulatory Process for the Review of Drugs for Rare Diseases |
11:30 AM – 12:00 PM | Committee Discussion |
12:00 PM – 1:00 PM | Lunch |
1:00 PM – 1:30 PM | Duchenne Muscular Dystrophy Evidence-Based Review: Update |
1:30 PM – 1:50 PM | Committee Discussion |
1:50 PM – 2:00 PM | Committee Liaison Update
|
2:00 PM – 2:20 PM | ACHDNC Decision Matrix Tool: Public Health System Assessment |
2:20 PM – 2:45 PM | Committee Discussion |
2:45 PM – 2:55 PM | Break |
2:55 PM – 3:10 PM | ACHDNC Nomination and Evidence Review Process |
3:10 PM – 3:30 PM | Committee Discussion |
3:30 PM – 3:45 PM | Awards and Acknowledgements |
3:45 PM | End Day 1 |
Friday, May 10, 2024, from 10:00 AM – 2:00 PM
(All times shown are in Eastern Time)
TIME | TOPIC |
10:00 AM – 10:15 AM |
|
10:15 AM – 10:35 AM | Qualitative Evidence Synthesis: GRADE-CERQual Approach For Assessing the Confidence in Synthesized Findings |
10:35 AM – 11:00 AM | Committee Discussion |
11:00 AM – 11:15 AM | Outcomes Research Criteria Update |
11:15 AM – 11:35 AM | Committee Discussion |
11:35 AM – 12:30 PM | Lunch |
12:30 PM – 1:45 PM | Newborn Screening Ad Hoc Topic Groups: Updates and Committee Discussion |
1:45 PM – 1:55 PM | New Business |
1:55 PM – 2:00 PM | Adjourn |